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Dernières publications
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Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
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A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
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Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
Chiffres clés
48
Publications with fulltext
Open Access
67 %
Mots clés
Animal/physiopathology
LncRNA
CaVβs
Dystrophine
Activin Receptors
Inhibitors
LncARN
Cell homeostasis
Becker BMD muscular dystrophy
Centronuclear myopathy
Muscle Strength
Calcium Channels
Molecular Sequence Data
MiARN
Ex-vivo
Inbred C57BL
Duchenne DMD dystrophy
Dystrophin-EGFP
Muscle
Muscle Biology
Antisense oligonucleotides
Muscular dystrophy
MES
Clinical trials
Multi exon skipping
Calcium
Drp1
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
Mdx mouse
Hear
Génomique
Cell Biology
DMO
Muscular Dystrophy
Humans
Dystrophie musculaire de Becker
L-Type
Dystrophin
Energy Metabolism/drug effects
Gene expression
Inbred mdx
DMD
CaV subunits
Immunoglobulin Fc Fragments/pharmacology
Delivery
BMD
DHPR α1S
Dystrophy
Dystrophie Musculaire de Becker BMD
NAD+
Metabolism
Gene Expression Regulation/drug effects
Human Umbilical Vein Endothelial Cells
Becker muscular dystrophy
CTNNB1
Liver
Exon skipping
Multiresolution modeling
Cardiomyopathie
Dynamin 2
Becker muscular dystrophy BMD
Cell Line
Muscles/physiopathology
LKB1
Genomic
Dystrophin central domain
Skeletal muscle
Mitochondrial fission
Duchenne muscular dystrophy
Gene modifiers
Muscular Atrophy
Diseases
Myotendinous junction
Long noncoding RNA
Cachexia
Homeostasis
Cardiomyopathy
Mice
Base Sequence
Allele‐specific silencing therapy
Modificateurs de gènes
Molecular docking
Knockout
Cells
Morphogenesis
Cultured
Epigenetics
CD38
Long QT
Hepatocellular carcinoma
Duchenne muscular dystrophy DMD
Animals
NNOS
Invivo
Dystrophie Musculaire de Duchenne DMD
Autophagy
Multi resolution modeling
Male
Muscle development
Myogenesis