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Mechanotransduction Cavéoles Myopathy Congenital myopathy Gene therapy Cell migration RNA interference Adeno-associated virus Autophagosome maturation Coeur Adhesion Cytoskeleton AAV Cellules de crête neurale Autophagy Autophagosome Cancer Dynamin overexpression Developmental biology Adeno-associated virus vector Nuclear envelope Muscle Cardiotoxin ACTN2 Alpha-actinin-2 Skeletal muscle Centronuclear myopathy Neural crest cells Nucleus Cell signaling Migration Lamin Dynamin Ctdnep1 AFM Duchenne muscular dystrophy Dystrophin Biomarkers Allele-specific silencing therapy CTL Caveolins Disease heterogeneity Dynamine Allele‐specific silencing therapy Correlative microscopy Charcot-Marie-Tooth Domaine LEM Atrial cardiac defects Amphiphysin Actin Allele specific RNA interference Adeno-Associated virus Dystrophie musculaire de Duchenne BAR proteins Clathrin Caveolin Animal models of human disease Cavins Allele-specific silencing Autosomal dominant centronuclear myopathy Caveolae Cross-bridge kinetics Cytosquelette Skin Atrial heart defects Endocytosis BMP signaling Cell proliferation AAV8 Myopathie Core myopathy Dominant centronuclear myopathy Biophysics Défauts cardiaques auriculaires Clathrine Nesprin Cellular neuroscience Developmental myosin heavy chain Satellite cell Disease modifiers DMyHC Diaphragm DNM2 Becker muscular dystrophy BMD Dystrophine CAV-3 gene Myosin Duchenne Muscular Dystrophy Muscular dystrophy Dystrophie musculaire d'Emery Dreifuss Outflow tract Dynamin 2 Antisense oligonucleotides AD-CNM Dullard Actin nucleus BAF Duchenne muscular dystrophy DMD Cross-presentation Adult patients